The Research Study
Currently Recruiting
15 Nov 2026
Up to $5,420
Melbourne, Australia
Friedreich’s Ataxia (FA) is a rare, inherited disease that affects the nervous system, muscles, and heart. Symptoms often begin in childhood or adolescence and can progressively impact balance, coordination, walking, speech, and daily activities. Over time, many people with FA experience increasing disability, and serious complications such as heart disease can occur.
FA is caused by a genetic change that reduces production of a protein called frataxin, which is essential for normal cell function. Because the underlying cause of FA is not fully addressed by current treatment options, there remains a significant need for new therapies that may help restore frataxin levels and potentially slow or modify disease progression.
We invite you to join our Phase 1 clinical study evaluating an investigative treatment for FA. By participating, you can offer hope to affected families and contribute to a future where FA no longer limits lives.
Join our clinical trial
This is not a first-in-human (FIH) study, meaning it is not the first time the potential treatment is being tested in people. The investigative therapy has been given to both healthy volunteers and FA patients. The study has been carefully designed with strict safety protocols and has been approved by an independent ethics committee. It is not known whether the study drug may cause unexpected, serious, or life-threatening side effects. While these are considered unlikely, you will be carefully monitored throughout the study and provided with prompt treatment if any such effects occur.
Before joining, you’ll receive detailed information about th e study, meet with a doctor, and have the chance to ask any questions.
What to expect
- Participation in a monitored clinical environment
- Study visits scheduled
- Support from a professional medical team
- Reimbursement for your time and commitment
Study schedule
| Intake 1 | In-clinic stay:
15 November 2026 – 23 November 2026 |
Follow-up visits:
25 November 2026
29 November 2026 6 December 2026
|
Study dates are subject to change. Our team will confirm details with you during the screening process.
Trial details
Study duration
- 8-night inpatient stay
- 3 follow-up visits
Study medication
The study drug will be administered in one of two ways: subcutaneous infusion or subcutaneous injection.
Additional eligibility
- Weigh less than or equal to 100kg at Screening
- No significant medical history
- Not taking any prescription medication
Ethics
An independent ethics committee has approved this clinical trial.
Are you a match?
Age
18 - 45 years old
Remuneration
Up to $5,420 *with screening reimbursement.
Full details outlined in consent form.
Gender
Male or Female
BMI
BMI 18 - 32 kg/m2
Commitment
8 nights, 3 clinic visits
Medical condition
Not taking any medications