Friedreich’s Ataxia (FA) is a rare, inherited disease that affects the nervous system, muscles, and heart. Symptoms often begin in childhood or adolescence and can progressively impact balance, coordination, walking, speech, and daily activities. Over time, many people with FA experience increasing disability, and serious complications such as heart disease can occur.
FA is caused by a genetic change that reduces production of a protein called frataxin, which is essential for normal cell function. Because the underlying cause of FA is not fully addressed by current treatment options, there remains a significant need for new therapies that may help restore frataxin levels and potentially slow or modify disease progression.
We invite you to join our Phase 1 clinical study evaluating an investigative treatment for FA. By participating, you can offer hope to affected families and contribute to a future where FA no longer limits lives.
Requirements
- Male or Female
- Healthy
- 18 - 45 years old
- BMI 18 - 32 kg/m2
- Not taking any medications
- Non-smoker or Occasional smoker
Study visits
8 nights, 3 clinic visits